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Familial hypercholesterolemia
Strict new guidelines lay out a path to heritable human gene editing | Science Newshttps://www.sciencenews.org/article/human-germline-gene-editing-crispr-strict-new-guidelines
Cystic fibrosisFamilial hypercholesterolemiaGene editing

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Familial hypercholesterolemia
Serum cholesterol